TheraRadar

Pharma Intelligence, Simplified

Data updated: Mar 10, 2026

GAVRETO

PRALSETINIB Rearranged during Transfection (RET) Inhibitors
Oncology Approved 2020-09-04

Gavreto (pralsetinib) is a kinase inhibitor indicated for the treatment of adult patients with metastatic non-small cell lung cancer (NSCLC) that is rearranged during transfection (RET) fusion-positive. It is also indicated for adult and pediatric patients aged 12 years and older with advanced or metastatic RET fusion-positive thyroid cancer. This therapy is reserved for thyroid cancer patients who require systemic therapy and are refractory to radioactive iodine treatment.

Source: FDA Label • BLUEPRINT MEDICINES • Kinase Inhibitor

How GAVRETO Works

Pralsetinib is a kinase inhibitor that targets wild-type RET as well as various oncogenic RET fusions and mutations. These genetic alterations can hyperactivate downstream signaling pathways, which leads to the uncontrolled proliferation of cancer cells. By inhibiting these specific proteins, the drug demonstrates anti-tumor activity and reduces the tumorigenic potential in cancers harboring RET fusions or mutations.

Source: FDA Label
3
Indications
--
Phase 3 Trials
2
Priority Reviews
5
Years on Market

Details

Status
Prescription
First Approved
2020-09-04
Routes
ORAL
Dosage Forms
CAPSULE

Companies

Active Ingredient: PRALSETINIB

GAVRETO Approval History

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What GAVRETO Treats

2 indications

GAVRETO is approved for 2 conditions since its original approval in 2020. These indications span multiple therapeutic areas including oncology, immunology, and more.

  • Metastatic RET fusion-positive non-small cell lung cancer
  • Advanced or metastatic RET fusion-positive thyroid cancer
Source: FDA Label

GAVRETO Boxed Warning

SERIOUS INFECTIONS, INCLUDING OPPORTUNISTIC INFECTIONS GAVRETO may increase the risk for serious infections, including bacterial, fungal, viral and opportunistic infections, which can lead to hospitalization or death. Withhold, reduce the dose or permanently discontinue GAVRETO based on severity [see Dosage and Administration (2.3) , Warnings and Precautions (5.1) ] . WARNING: SERIOUS INFECTIONS, INCLUDING OPPORTUNISTIC INFECTIONS See full prescribing information for complete boxed warning. GAVR...

GAVRETO Target & Pathway

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Target

JAK1 (Janus Kinase 1) Intracellular Kinase

A member of the JAK family involved in signaling for interferons and several interleukins. JAK1 inhibition is effective in rheumatoid arthritis, atopic dermatitis, and other inflammatory conditions by blocking multiple cytokine pathways.

GAVRETO Competitors

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6 other drugs also target FGFR1. Compare mechanisms, indications, and trial activity.

Drug = Competitor name Company = Manufacturer N indic. = FDA-approved indications → Date = Patent/exclusivity expiry

Competitors share the same molecular target (FGFR1). Earlier expiry dates signal biosimilar/generic opportunities.

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Active Pipeline

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Ongoing clinical trials by development phase

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Key Completed Trials

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Completed studies with published results, ranked by significance

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Trial Timeline

Full development history with FDA approval milestones

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Understanding FDA Approval Types
Count Type What it means
- ORIG Original approval - drug first enters market
- SUPPL - Efficacy New indication (new disease/condition approved)
- SUPPL - Labeling Label text changes (warnings, dosing updates)
- SUPPL - Manufacturing Production changes (new facility)
- SUPPL - Chemistry Formulation changes (new dosage strength)

Green lines in the timeline show ORIG and Efficacy approvals - the clinically meaningful milestones.

GAVRETO FDA Label Details

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Indications & Usage

FDA Label (PDF)

GAVRETO is a kinase inhibitor indicated for treatment of: Adult patients with metastatic rearranged during transfection (RET ) fusion-positive non-small cell lung cancer as detected by an FDA approved test (NSCLC). Adult and pediatric patients 12 years of age and older with advanced or metastatic RET fusion-positive thyroid cancer who require systemic therapy and who are radioactive iodine-refractory (if radioactive iodine is appropriate). This indication is approved under accelerated approval based on overall response rate and duration of response. Continued approval for this indication may b...

⚠️ BOXED WARNING

WARNING: SERIOUS INFECTIONS, INCLUDING OPPORTUNISTIC INFECTIONS GAVRETO may increase the risk for serious infections, including bacterial, fungal, viral and opportunistic infections, which can lead to hospitalization or death. Withhold, reduce the dose or permanently discontinue GAVRETO based on sev...

GAVRETO Patents & Exclusivity

Latest Patent: Apr 2039
Exclusivity: Nov 2027

Patents (5 active)

US11273160 Expires Apr 3, 2039
US11872192 Expires Apr 3, 2039
US11963958 Expires Apr 3, 2039
US10030005 Expires Nov 1, 2036

Exclusivity

ODE-318 Until Sep 2027
ODE-340 Until Dec 2027
ODE-341 Until Dec 2027
Source: FDA Orange Book

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Data Sources

Data sourced from official FDA and NIH databases. Click links to verify on original sources.